La dernière actualité médicale en hémophilie Consultez la version en ligne |
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Mercredi 09 octobre 2024 |
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Bonjour
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Découvrez ci-dessous la dernière actualité scientifique dans votre domaine d'expertise, issue des plus prestigieuses revues à comité de lecture. |
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Actualités cliniques |
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Haemophilia 2023; 29(6): 1442-9 | Ana Boban
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Haemophilia is a rare inherited bleeding disorder characterised by spontaneous bleeding and chronic impairment of musculoskeletal system. Due to its rarity and complexity, haemophilia is best managed by... |
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Orphanet Journal of Rare Diseases 2024; 19(1): 59 | Fletcher Simon et al. |
Gene therapy offers people with haemophilia (PwH) the potential of a life free from prophylactic factor replacement therapy and spontaneous joint bleeding [1, 2]. The availability of gene therapy for haemophilia... |
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